Research Articles
AAV Gene Therapy Rescues Cellular Chaos in Rare Muscle Disease
Breakthrough research shows AAV-based TCAP delivery rescues mitochondria dislocation in limb-girdle muscular dystrophy R7, offering new hope for rare disease treatment.
The Invisible Scaffold: How Decoding Muscle's Hidden Architecture Revolutionized Duchenne Muscular Dystrophy Treatment
Explore the groundbreaking research on subsarcolemmal cytoskeleton and dystrophin that transformed our understanding and treatment of Duchenne Muscular Dystrophy.
The Dystrophin Breakthrough: Solving Duchenne's Deadly Mystery
How the discovery of dystrophin transformed our understanding of Duchenne Muscular Dystrophy and paved the way for modern therapies.